Publications
publications by categories in reversed chronological order. generated by jekyll-scholar.
2023
- Simultaneous inhibition of DNA-PK and Polϴ improves integration efficiency and precision of genome editingNature communications, 2023
- A Type II-B Cas9 nuclease with minimized off-targets and reduced chromosomal translocations in vivoNature Communications, 2023
2022
- DNA Repair Pathways in the Context of Therapeutic Genome EditingGenome Editing in Drug Discovery, 2022
- Tools for efficient genome editing; ZFN, TALEN, and CRISPRApplications of genome modulation and editing, 2022
2019
- In vivo genome and base editing of a human PCSK9 knock-in hypercholesterolemic mouse modelBMC biology, 2019
2018
- Therapeutic genome editing with CRISPR/Cas9 in a humanized mouse model ameliorates \alpha1-antitrypsin deficiency phenotypeEBioMedicine, 2018
- Decoding non-random mutational signatures at Cas9 targeted sitesNucleic acids research, 2018